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Research Database PMU-SQQUID

EBNER PATRICIA
Research Management at Paracelsus Medical University

Publications | Researcher Profile

66 Publications

2023

Journal Articles

COL7A1 Editing via RNA Trans-Splicing in RDEB-Derived Skin Equivalents.
Liemberger, B; Bischof, J; Ablinger, M; Hainzl, S; Murauer, EM; Lackner, N; Ebner, P; Kocher, T; Nyström, A; Wally, V; Mayr, E; Guttmann-Gruber, C; Hofbauer, JP; Bauer, JW; Koller, U;
Int J Mol Sci. 2023; 24(5):
Full papers/articles (Journal)

2022

Journal Articles

Synergy of Human Platelet-Derived Extracellular Vesicles with Secretome Proteins Promotes Regenerative Functions.
Gomes, FG; Andrade, AC; Wolf, M; Hochmann, S; Krisch, L; Maeding, N; Regl, C; Poupardin, R; Ebner-Peking, P; Huber, CG; Meisner-Kober, N; Schallmoser, K; Strunk, D;
Biomedicines. 2022; 10(2):
Full papers/articles (Journal)
Extra-hematopoietic immunomodulatory role of the guanine-exchange factor DOCK2.
Scharler, C; Poupardin, R; Ebner-Peking, P; Wolf, M; Schreck, C; Brachtl, G; Cronemberger Andrade, A; Krisch, L; Daheron, L; Schallmoser, K; Jürchott, K; Küchler, J; Stachelscheid, H; Volk, HD; Oostendorp, RAJ; Strunk, D;
Commun Biol. 2022; 5(1): 1246
Full papers/articles (Journal)
A functional corona around extracellular vesicles enhances angiogenesis, skin regeneration and immunomodulation.
Wolf, M; Poupardin, RW; Ebner-Peking, P; Andrade, AC; Blöchl, C; Obermayer, A; Gomes, FG; Vari, B; Maeding, N; Eminger, E; Binder, HM; Raninger, AM; Hochmann, S; Brachtl, G; Spittler, A; Heuser, T; Ofir, R; Huber, CG; Aberman, Z; Schallmoser, K; Volk, HD; Strunk, D;
J Extracell Vesicles. 2022; 11(4): e12207
Full papers/articles (Journal)

2021

Journal Articles

Hypoxic Conditions Promote the Angiogenic Potential of Human Induced Pluripotent Stem Cell-Derived Extracellular Vesicles.
Andrade, AC; Wolf, M; Binder, HM; Gomes, FG; Manstein, F; Ebner-Peking, P; Poupardin, R; Zweigerdt, R; Schallmoser, K; Strunk, D;
Int J Mol Sci. 2021; 22(8):
Full papers/articles (Journal)
Scalable Enrichment of Immunomodulatory Human Acute Myeloid Leukemia Cell Line-Derived Extracellular Vesicles.
Binder, HM; Maeding, N; Wolf, M; Cronemberger Andrade, A; Vari, B; Krisch, L; Gomes, FG; Blöchl, C; Muigg, K; Poupardin, R; Raninger, AM; Heuser, T; Obermayer, A; Ebner-Peking, P; Pleyer, L; Greil, R; Huber, CG; Schallmoser, K; Strunk, D;
Cells. 2021; 10(12):
Full papers/articles (Journal)
Self-assembly of differentiated progenitor cells facilitates spheroid human skin organoid formation and planar skin regeneration
Ebner-Peking, P; Krisch, L; Wolf, M; Hochmann, S; Hoog, A; Vari, B; Muigg, K; Poupardin, R; Scharler, C; Schmidhuber, S; Russe, E; Stachelscheid, H; Schneeberger, A; Schallmoser, K; Strunk, D
THERANOSTICS. 2021; 11(17): 8430-8447.
Full papers/articles (Journal)
Improving Human Induced Pluripotent Stem Cell-Derived Megakaryocyte Differentiation and Platelet Production.
Krisch, L; Brachtl, G; Hochmann, S; Andrade, AC; Oeller, M; Ebner-Peking, P; Schallmoser, K; Strunk, D;
Int J Mol Sci. 2021; 22(15):
Full papers/articles (Journal)

Conference papers, proceedings, abstracts

Development of a non-invasive and non-viral in vivo RNA therapy approach for dystrophic epidermolysis bullosa
Liemberger, B; Kocher, T; Lettner, T; Ablinger, M; Reichl, V; Lackner, N; Peking, P; Murauer, EM; Nystrom, A; Wally, V; Mayr, E; Guttmann-Gruber, C; Bauer, JW; Koller, U
EXP DERMATOL. 2021; 30(3): E43-E43.
Abstracts (Journal)

Unpublished conference presentations

Extracellular vesicles derived from induced pluripotent stem cells in hypoxic conditions enhance angiogenesis.
Cronemberger, A; Wolf, M; Binder HM; Gueths Gomes F; Manstein, F; Ebner P; Poupardin, R; Zweigerdt, R; Schallmoser, K; Strunk, D
ISEV Massive EV-Workshop 2021; 28.-29.10.2021; Desenzano. 2021.
Extracellular vesicles derived from induced pluripotent stem cells in hypoxic conditions enhance angiogenesis.
Cronemberger, A; Wolf, M; Binder HM; Gueths Gomes F; Manstein, F; Ebner P; Poupardin, R; Zweigerdt, R; Schallmoser, K; Strunk, D
ASEV Young Scientist Meeting 2021; 15.-16.10.2021; Krems. 2021.
Extracellular vesicles derived from induced pluripotent stem cells in hypoxic conditions enhance angiogenesis.
Cronemberger, A; Wolf, M; Binder HM; Gueths Gomes F; Manstein, F; Ebner P; Poupardin, R; Zweigerdt, R; Schallmoser, K; Strunk, D
Paracelsus Virtual Science Get Together 2021 – 2. Virtual Science Summer ; 01.07.-01.10.2021; online. 2021.
Extracellular vesicles derived from induced pluripotent stem cells in hypoxic conditions enhance angiogenesis.
Cronemberger, A; Wolf, M; Binder HM; Gueths Gomes F; Manstein, F; Ebner P; Poupardin, R; Zweigerdt, R; Schallmoser, K; Strunk, D:
4th GSEV 2021 Autumn Meeting; 03.-04.10.2021; Freiburg im Breisgau. 2021.
Human platelet lysate for skin regeneration & immune modulation.
Fausto Gueths Gomes, André Cronemberger Andrade, Martin Wolf, Sarah Hochmann, Linda Krisch, Nicole Maeding, Christof Regl, Patricia Ebner-Peking, Christian Huber, Nicole Meisner-Kober, Katharina Schallmoser, Dirk Strunk
ASEV Young Scientist Meeting 2021; ; 15.-16.10.2021; Krems. 2021.
Human Platelet Lysate for Skin Regeneration & Immune Modulation.
Gueths Gomes, F; Cronemberger A; Wolf, M; Hochmann, S; Krisch, L; Regl, C; Ebner, P; Huber, C; Meisner-Kober, N; Schallmoser, K; Strunk, D
Paracelsus Virtual Science Get Together 2021 – 2. Virtual Science Summer; 01.07.-01.10.2021; online. 2021.
Mesoderm induction improves human induced pluripotent stem cell-derived megakaryocyte differentiation and platelet production.
Krisch, L; Brachtl, G; Hochmann, S; Cronemberger A; Ebner-Peking, P; Öller, M; Schallmoser, K; Strunk, D
Paracelsus Virtual Science Get Together 2021 – 2. Virtual Science Summer ; 01.07.-01.10.2021; online. 2021.
Enhanced angiogenesis and wound healing in vivo induced by extracellular vesicles from therapeutic grade allogeneic human placental stromal cells.
Martin Wolf, Rodolphe Poupardin, Constantin Blöchl, Andre Cronemberger Andrade, Fausto Gueths Gomes, Patrica Peking , Balazs Vari, Essi Eminger; Heide-Marie Binder, Anna M Raninger, Gabi Brachtl, Andreas Spittler, Thomas Heuser, Astrid Obermayer, Christian G Huber, Katharina Schallmoser, Hans-Dieter Volk, Dirk Strunk
10th Annual Meeting ISEV 2021; 18.-21.05.2021; online. 2021.
First evidence for a protein corona around extracellular vesicles playing an essential role in aiding angiogenesis and skin regeneration.
Martin Wolf, Rodolphe W Poupardin, Patricia Ebner-Peking, André Cronemberger Andrade, Constantin Blöchl, Astrid Obermayer, Fausto Gueths Gomes,, Balazs Vari, Essi Eminger, Heide-Marie Binder, Anna M Raninger, Sarah Hochmann, Gabriele Brachtl, Andreas Spittler, Thomas Heuser, Racheli Ofir, Christian G Huber, Zami Aberman, Katharina Schallmoser, Hans-Dieter Volk, Dirk Strunk
ASEV Young Scientist Meeting 2021; 15.-16.10.2021; Krems. 2021.
Essential role of a protein corona around extracellular vesicles in aiding angiogenesis and skin regeneration.
Martin Wolf, Rodolphe W Poupardin, Patricia Ebner-Peking, André Cronemberger Andrade, Constantin Blöchl, Astrid Obermayer, Fausto Gueths Gomes,, Balazs Vari, Essi Eminger, Heide-Marie Binder, Anna M Raninger, Sarah Hochmann, Gabriele Brachtl, Andreas Spittler, Thomas Heuser, Racheli Ofir, Christian G Huber, Zami Aberman, Katharina Schallmoser, Hans-Dieter Volk, Dirk Strunk
GSEV Meeting 2021; 03.-04.10.2021; Freiburg. 2021.
Self-assembly of human iPSC-derived single cells creates skin organoids and regenerates vascularized human skin.
Patricia Ebner, Linda Krisch, Martin Wolf, Anna Hoog, Sarah Hochmann, Balázs Vári, Katharina Muigg, Rodolphe Poupardin, Cornelia Scharler, Sabine Schmidhuber, Elisabeth Russe, Cornelia Hauser-Kronberger, Harald Stachelscheid, Achim Schneeberger, Katharina Schallmoser, Dirk Strunk
Paracelsus Virtual Science Get Together 2021 – 2. Virtual Science Summer; 01.07.-01.10.2021; online. 2021.

2020

Conference papers, proceedings, abstracts

TOWARDS PRODUCTION OF IPSC-DERIVED HUMAN PLATELETS FOR REGENERATIVE PURPOSES
L Krisch, M Oeller, C Scharler, P Peking, A Hoog, E Rohde, D Strunk
Vox Sanguinis. 2020; 115 (Suppl. s1): 364-364.-ISBT; 12.-16.12.2020; Virtual Conference.
Abstracts (Journal)

Unpublished conference presentations

Self-assembly of iPSC-derived human vascularized human skin and skin organoids.
Peking, P; Hoog, A; Wolf, M; Scharler, C; Vári, B; Russe, E; Krisch, L; Schallmoser, K; Strunk, D
24. Jahressymposium der IGLD; 05.-07.03.2020; Frankfurt. 2020.

2019

Journal Articles

Gene Editing-Mediated Disruption of Epidermolytic Ichthyosis-Associated KRT10 Alleles Restores Filament Stability in Keratinocytes.
March, OP; Lettner, T; Klausegger, A; Ablinger, M; Kocher, T; Hainzl, S; Peking, P; Lackner, N; Rajan, N; Hofbauer, JP; Guttmann-Gruber, C; Bygum, A; Koller, U; Reichelt, J;
J Invest Dermatol. 2019; 139(8): 1699-1710.e6.
Full papers/articles (Journal)
An ex vivo RNA trans-splicing strategy to correct human generalized severe epidermolysis bullosa simplex.
Peking, P; Breitenbach, JS; Ablinger, M; Muss, WH; Poetschke, FJ; Kocher, T; Koller, U; Hainzl, S; Kitzmueller, S; Bauer, JW; Reichelt, J; Lettner, T; Wally, V;
Br J Dermatol. 2019; 180(1):141-148
Full papers/articles (Journal)

Conference papers, proceedings, abstracts

Immune suppression for xeno-cell transplantation strategies in the porcine animal model
Demkes, EJ; Peking, P; van Oostveen, M; de Jager, SCA; Bijsterveld, MPA; Halloin, C; Haase, A; Martin, U; Doevendans, PAF; H?fer, IE; Zweigerdt, R; Strunk, D; Sluijter, JPG
HUM GENE THER. 2019; 30(8): A15-A15.
Abstracts (Journal)
Gene editing as a therapeutic option for epidermolytic ichthyosis
March, OP; Lettner, T; Klausegger, A; Ablinger, M; Kocher, T; Hainzl, S; Peking, P; Lackner, N; Aushev, M; Koller, U; Reichelt, J
EXP DERMATOL. 2019; 28(3): E45-E45.
Abstracts (Journal)

Unpublished conference presentations

How to select the appropriate cell sorting strategy.
Hoog, A; Raninger, AM; Peking, P; Brachtl, G; Strunk D;
SCI-TReCS Retreat 2019; 16.-17.09.2019; Wagrain. 2019.
Optimizing Culture Conditions for the Production of iPSC-derived Megakaryocytes
Krisch, L; Oeller, M; Scharler, C; Peking, P; Strunk, D; Schallmoser, K
SCI-TReCS Retreat 2019; 16.-17.09.2019; Wagrain. 2019.
Enhancement of stem cell differentiation by environmental cues.
Muigg, K; Hoog, A; Scharler, C; Öller, M; Peking, P; Schallmoser, K; Strunk D;
SCI-TReCS Retreat 2019; 16.-17.09.2019; Wagrain. 2019.
Enhancement of human pluripotent stem cell differentiation by environmental cues.
Muigg, K; Hoog, A; Scharler, C; Öller, M; Peking, P; Strunk, D;
Technobeat Symposium Hannover; 02.-04.12.2019; Hannover. 2019.
Self-assembly of stem/progenitor cells creates human neo-vascularized skin and skin organoids.
Peking, P;
7th Annual GSCN Conference; 23.-25.09.2019; Berlin. 2019.
Development of a human 3D vascularized skin organoid model.
Peking, P; Hochreiter, A; Scharler, C; Vári, B; Wimmer, M; Krisch, L; Wolf, M; Hochmann, S; Schallmoser, K; Strunk, D
ISSCR International Symposium; 20.-22.02.2019; Amsterdam. 2019.
Self-Assembly of human neo-vascularized skin and skin organoids.
Peking, P; Hochreiter, A; Wolf, M; Scharler, C; Vári, B; Krisch, L; Schallmoser, K; Strunk, D
ISSCR Annual Meeting; 26.-29.06.2019; Los Angeles. 2019.
Self-assembly of stem/progenitor cells creates human neo-vascularized skin and skin organoids.
Peking, P; Hoog, A; Wolf, M; Vári, B; Sonderegger, A; Scharler, C; Russe, E; Krisch, L; Schallmoser, K; Strunk, D
ESGCT 27th Annual Congress; 22.-25.10.2019; Barcelona. 2019.
iPSC-based Skin Regeneration.
Peking, P; Hoog, A; Wolf, M; Vári, B; Sonderegger, A; Scharler, C; Russe, E; Krisch, L; Schallmoser, K; Strunk, D;
SCI-TReCS Retreat 2019; 16.-17.09.2019; Wagrain. 2019.
Self-assembly of stem/progenitor cells creates human neo-vascularized skin and skin organoids.
Peking, P; Hoog, A; Wolf, M; Vári, B; Sonderegger, A; Scharler, C; Russe, E; Krisch, L; Schallmoser, K; Strunk, D;
RESTORE 1st Advanced Therapies Science Meeting; 25.-26.11.2019; Berlin. 2019.
Self-assembly of stem/progenitor cells creates human neo-vascularized skin and skin organoids.
Peking, P; Hoog, A; Wolf, M; Vári, B; Sonderegger, A; Scharler, C; Russe, E; Krisch, L; Schallmoser, K; Strunk, D;
7th Annual GSCN Conference; 23.-25.09.2019; Berlin. 2019.
Self-assembly of stem/progenitor cells creates human neo-vascularized skin and skin organoids.
Peking, P; Hoog, A; Wolf, M; Vári, B; Sonderegger, A; Scharler, C; Russe, E; Krisch, L; Schallmoser, K; Strunk D;
7th Annual GSCN Conference; 23.-25.09.2019; Berlin. 2019.
Self-assembly of stem/progenitor cells creates human neo-vascularized skin and skin organoids.
Peking, P; Hoog, A; Wolf, M; Vári, B; Sonderegger, A; Scharler, C; Russe, E; Krisch, L; Schallmoser, K; Strunk D;
SCI-TReCS Retreat 2019; 16.-17.09.2019; Wagrain. 2019.
3D cartilage regeneration capacity of different stromal progenitor cells.
Sonderegger, A; Hochmann, S; Mittermeir, M; Peking, P; Wolf, M; Poupardin P; Strunk D;
SCI TReCS Retreat 2019; 16.-17.09.2019; Wagrain. 2019.

2018

Journal Articles

ÖGDV Preisträger stellen sich vor: Der Wissenschaftspreis der ÖGDV 2017 ging an Dr. rer. nat. Stefan Hainzl und Dr. rer. nat. Patricia Peking aus Salzburg.
Hainzl, S; Peking, P;
J Dtsch Dermatol Ges. 2018; 16(4): 527-528.
Notes
Functional therapies for cutaneous wound repair in epidermolysis bullosa.
Peking, P; Koller, U; Murauer, EM;
Adv Drug Deliv Rev. 2018; 129:330-343
Full papers/articles (Journal)

Conference papers, proceedings, abstracts

TALEN-mediated inactivation of dominant-negative keratin alleles results in the formation of a stable functional cytoskeleton and phenotypic alleviation of epidermolytic ichthyosis
March, OP; Kocher, T; Lettner, T; Ablinger, M; Lackner, N; Hainzl, S; Peking, P; Aushev, M; Koller, U; Reichelt, J
J INVEST DERMATOL. 2018; 138(5): S138-S138.
Abstracts (Journal)
Generation of immunosuppressive iPSC-derived stromal cells for tissue regeneration
Scharler, C; Peking, P; Ketterl, N; Hochreiter, A; Juerchott, K; Brachtl, G; Wimmer, M; Hochmann, S; Wolf, M; Schallmoser, K; Volk, HD; Strunk, D
HUM GENE THER. 2018; 29(12): A56-A56.
Abstracts (Journal)
Generation of immunosuppressive iPSC-derived stromal cells for tissue regeneration
Scharler, C; Peking, P; Ketterl, N; Hochreiter, A; Jurchott, K; Brachtl, G; Wimmer, M; Hochmann, S; Wolf, M; Schallmoser, K; Volk, HD; Strunk, D
HUM GENE THER. 2018; 29(12): A56-A56.
Abstracts (Journal)

Unpublished conference presentations

Development of a human 3D vascularized skin organoid model.
Peking, P; Hochreiter, A; Scharler, C; Wimmer, M; Krisch, L; Wolf, M; Hochmann, S; Schallmoser, K; Strunk, D
6th Annual GSCN Conference; 19.-21.09.2018; Heidelberg. 2018.
Development of an iPSC-mediated strategy for skin regeneration.
Peking, P; Hochreiter, A; Scharler, C; Wimmer, M; Krisch, L; Wolf, M; Hochmann, S; Schallmoser, K; Strunk, D
SCI-TReCS Retreat 2018; 13.-14.09.2018; Wagrain. 2018.
Development of a human 3D vascularized skin organoid model.
Peking, P; Hochreiter, A; Scharler, C; Wimmer, M; Krisch, L; Wolf, M; Hochmann, S; Schallmoser, K; Strunk, D
SCI-TReCS Retreat 2018; 13.-14.09.2018; Wagrain. 2018.
Development of an iPSC-mediated strategy for skin regeneration.
Peking, P; Hochreiter, A; Scharler, C; Wimmer, M; Krisch, L; Wolf, M; Hochmann, S; Schallmoser, K; Strunk, D
2018 ESDR Future Leaders Academy; 03.-05.10.2018; Budapest. 2018.
Development of immunosuppressive iPSC-derived stromal cells for tissue regeneration.
Peking, P; Scharler, C; Ketterl, N; Hochreiter, A; Jürchott, K; Höfler, M; Brachtl, G; Wimmer, M; Wolf, M; Hochmann, S; Schallmoser, K; Volk, H-D; Strunk, D
6th Annual GSCN Conference; 19.-21.09.2018; Heidelberg. 2018.
Generation of immunosuppressive iPSC-derived stromal cells for tissue regeneration.
Scharler, C; Peking, P; Ketterl, N; Hochreiter, A; Jürchott, K; Höfler, M; Brachtl, G; Wimmer, M; Wolf, M; Hochmann, S; Schallmoser, K; Volk, HD; Strunk, D
26th Annual Congress of the ESGCT; 16.-19.10.2018; Lausanne. 2018.

2017

Journal Articles

RNA-based therapies for genodermatoses.
Bornert, O; Peking, P; Bremer, J; Koller, U; van den Akker, PC; Aartsma-Rus, A; Pasmooij, AM; Murauer, EM; Nyström, A;
Exp Dermatol. 2017; 26(1):3-10
Reviews
COL7A1 Editing via CRISPR/Cas9 in Recessive Dystrophic Epidermolysis Bullosa.
Hainzl, S; Peking, P; Kocher, T; Murauer, EM; Larcher, F; Del Rio, M; Duarte, B; Steiner, M; Klausegger, A; Bauer, JW; Reichelt, J; Koller, U;
Mol Ther. 2017; 25(11):2573-2584
Full papers/articles (Journal)
Cut and Paste: Efficient Homology-Directed Repair of a Dominant Negative KRT14 Mutation via CRISPR/Cas9 Nickases.
Kocher, T; Peking, P; Klausegger, A; Murauer, EM; Hofbauer, JP; Wally, V; Lettner, T; Hainzl, S; Ablinger, M; Bauer, JW; Reichelt, J; Koller, U;
Mol Ther. 2017; 25(11):2585-2598
Full papers/articles (Journal)
An RNA-targeted therapy for dystrophic epidermolysis bullosa.
Peking, P; Koller, U; Duarte, B; Murillas, R; Wolf, S; Maetzig, T; Rothe, M; Kocher, T; García, M; Brachtl, G; Schambach, A; Larcher, F; Reichelt, J; Bauer, JW; Murauer, EM;
Nucleic Acids Res. 2017; 45(17): 1025-10269.
Full papers/articles (Journal)
ADF Winter School-An exciting concept of the Arbeitsgemeinschaft Dermatologische Forschung to connect young scientists and clinician scientists in Dermatology at the top of Germany.
Yazdi, AS; Barlin, M; Böhm, K; Gendrisch, F; Ghorbanalipoor, S; Häberle, S; Hamel, A; Hüning, S; Hüttner, C; Iwanova, I; Kanaki, T; Kimeswenger, S; Lohmann, N; Munir, S; Muzumdar, S; Pereira, MP; Peking, P; Plesser, K; Rendon, A; Rentschler, M; Schlumprecht, C; Smorodchenko, A; Stock, M; Tillmanns, J; Uslu, U; Ghoreschi, K; Glatz, M; Grabbe, S; Kunz, M; Ludwig, R; Scharffetter-Kochanek, K; Loser, K;
Exp Dermatol. 2017; 26(3): 292-294.
Notes

Conference papers, proceedings, abstracts

Ex vivo COL7A1 editing via CRISPR/Cas9 in recessive dystrophic epidermolysis bullosa
Hainzl, S; Peking, P; Kocher, T; Murauer, E; Larcher, F; Duarte, B; Steiner, M; Bauer, J; Reichelt, J; Koller, U
J INVEST DERMATOL. 2017; 137(5): S92-S92.
Abstracts (Journal)
Improved safety profile: An efficient CRISPR/Cas9 double nicking approach for KRT14 repair in EB simplex
Kocher, T; Peking, P; Klausegger, A; Murauer, EM; Hofbauer, JP; Wally, V; Lettner, T; Hainzl, S; Ablinger, M; Bauer, JW; Reichelt, J; Koller, U
J INVEST DERMATOL. 2017; 137(10): S225-S225.
Abstracts (Journal)
Highly efficient and safe CRISPR/Cas9n double nicking-mediated KRT14 repair in epidermolysis bullosa simplex keratinocytes
Kocher, T; Peking, P; Klausegger, A; Murauer, EM; Hofbauer, JP; Wally, V; Lettner, T; Hainzl, S; Ablinger, M; Bauer, JW; Reichelt, J; Koller, U
HUM GENE THER. 2017; 28(12): A57-A57.
Abstracts (Journal)

2016

Journal Articles

A Gene Gun-mediated Nonviral RNA trans-splicing Strategy for Col7a1 Repair.
Peking, P; Koller, U; Hainzl, S; Kitzmueller, S; Kocher, T; Mayr, E; Nyström, A; Lener, T; Reichelt, J; Bauer, JW; Murauer, EM;
Mol Ther Nucleic Acids. 2016; 5: e287
Full papers/articles (Journal)

Conference papers, proceedings, abstracts

A murine transplantation model for trans-splicing corrected human keratinocytes
Ablinger, M; Breitenbach, JS; Lettner, T; Muss, W; Peking, P; Hainzl, S; Kocher, T; Kitzmuller, SK; Reichelt, J; Bauer, JW; Wally, V
HUM GENE THER. 2016; 27(11): A184-A184.
Abstracts (Journal)
Long-term in vivo correction of a recessive dystrophic epidermolysis bullosa phenotype using RNA trans-splicing repair
Peking, P; Koller, U; Duarte, BG; Wolf, S; Murrillas, R; Diez, MG; Schambach, A; Larcher, F; Bauer, JW; Murauer, EM
J INVEST DERMATOL. 2016; 136(9): S189-S189.
Abstracts (Journal)

2015

Conference papers, proceedings, abstracts

Trans-splicing gene therapy in the KRT14 gene
Breitenbach, JS; Lettner, T; Kocher, T; Muss, W; Peking, P; Hainzl, S; Kitzmuller, SK; Ablinger, M; Potschke, FJ; Bauer, JW; Wally, V
HUM GENE THER. 2015; 26(10): A44-A44.
Abstracts (Journal)
Correction of type VII collagen in a murine recessive dystrophic epidermolysis bullosa model using RNA trans-splicing
Peking, P; Koller, U; Hainzl, S; Kocher, T; Mayr, E; Kitzmuller, S; Lener, T; Bruckner-Tudermann, L; Bauer, JW; Murauer, EM
HUM GENE THER. 2015; 26(10): A48-A48.
Abstracts (Journal)

2014

Conference papers, proceedings, abstracts

Correction of type VII collagen in dystrophic epidermolysis bullosa by novel trans-splicing molecules
Peking, P; Mayr, E; Koller, U; Hainzl, S; Kocher, T; Bauer, JW; Murauer, EM
J INVEST DERMATOL. 2014; 134: S56-S56.
Abstracts (Journal)

2013

Journal Articles

The pathogenetic role of IL-1β in severe epidermolysis bullosa simplex.
Wally, V; Lettner, T; Peking, P; Peckl-Schmid, D; Murauer, EM; Hainzl, S; Hintner, H; Bauer, JW;
J Invest Dermatol. 2013; 133(7):1901-1903
Letters